Genetic Disorder 归档 - GenRNA Vision

Genetic Disease

Genetic Diseases in Active Gene Editing Clinical Trials and Progress

Genetic Diseases in Active Gene Editing Clinical Trials and Progress (As of May 2025, based on global clinical trial data) I. Hematologic Disorders 1. Sickle Cell Disease (SCD) & β-Thalassemia Candidate Therapies: exa-cel (CTX001): Co-developed by CRISPR Therapeutics and Vertex, this therapy act…

0评论

2025年5月17日

Genetic Diseases Treatable with Gene Editing and Key Case Studies

Genetic Disorder

CRISPR / Gene / Genetic Disorder

Genetic Diseases Treatable with Gene Editing and Key Case Studies

Genetic Diseases Treatable with Gene Editing and Key Case Studies (As of May 2025) Gene editing technologies, particularly CRISPR-Cas9, have enabled precise interventions for monogenic disorders while making breakthroughs in polygenic diseases, mitochondrial disorders, and rare conditions. Below is …

0评论

2025年5月17日